This article is a case analysis on rare disease drug security. Through the case analysis of SMA patients, it explores the current situation and difficulties of rare disease drug security. SMA patients face problems such as difficult diagnosis, low drug accessibility, and insufficient daily management, and need more help and care from the government and society. It also introduces some local security models and experiences, providing a reference for solving the problem of rare disease drug security.
初审：中文：田娜莹
英文：马林玥
复审：董田甜
